Dystrophie musculaire de Duchenne Dystrophie musculaire de Duchenne Dystrophie musculaire de Duchenne

News

FDA Acceptance of Casimersen
By Marie
In News, Treatments
Posted 26 August 2020

FDA Acceptance of Casimersen

Sarepta Therapeutics Announces FDA Acceptance of Casimersen (SRP-4045) New Drug Application for Patients with Duchenne Muscular Dystrophy Amenable to Skipping Exon 45 Original press release, [...]

Viltolarsen, exon 53 skipping therapy, approved
By Marie
In News, Research, Treatments
Posted 13 August 2020

Viltolarsen, exon 53 skipping therapy, approved

N.S. Pharma’s VILTEPSO™ (viltolarsen) injection now FDA-Approved in the U.S. for the treatment of Duchenne muscular dystrophy in patients amenable to exon 53 skipping therapy.   Patients [...]

Translarna: Update for Non-Ambulatory Patients with DMD
By Marie
In News, Treatments
Posted 29 June 2020

Translarna: Update for Non-Ambulatory Patients with DMD

PTC Therapeutics Announces that The Committee for Medicinal Products for Human Use (CHMP) Recommendation of Translarna ™ (ataluren) Label Update for Non-Ambulatory Patients with Duchenne Muscular [...]

Sarepta is seeking the approval of casimersen for DMD patients
By Marie
In News, Research, Treatments
Posted 26 June 2020

Sarepta is seeking the approval of casimersen for DMD patients

Sarepta Therapeutics Completes Submission of New Drug Application Seeking Approval of Casimersen (SRP-4045) for Patients with Duchenne Muscular Dystrophy Amenable to Skipping Exon 45 Casimersen [...]

Positive Safety and Efficacy Data from Micro-Dystrophin Gene Therapy
By Marie
In News, Research
Posted 16 June 2020

Positive Safety and Efficacy Data from Micro-Dystrophin Gene Therapy

Sarepta Therapeutics Announces Positive Safety and Efficacy Data from the SRP-9001 Micro-Dystrophin Gene Therapy Trial Published in JAMA Neurology   Press release here > CAMBRIDGE, Mass., [...]

Press release from Pfizer about gene therapy
By Marie
In News, Research, Treatments
Posted 15 May 2020

Press release from Pfizer about gene therapy

Pfizer’s new phase 1b results of gene therapy in ambulatory boys with Duchenne muscular dystrophy (DMD) support advancement into pivotal phase 3 study Read the press release here. Friday, [...]

Latest edition of the Catabasis Connection newsletter
By Marie
In News, Research, Treatments
Posted 12 May 2020

Latest edition of the Catabasis Connection newsletter

La Force is happy to share the latest edition of the Catabasis Connection newsletter with updates on edasalonexent and information that Catabasis shared at the MDA Virtual Poster Session. Earlier [...]

COVID-19 for people affected by Duchenne or Becker #3
By Marie
In News
Posted 3 April 2020

COVID-19 for people affected by Duchenne or Becker #3

What we know about COVID-19 part 3 What do we know about COVID-19 for people affected by Duchenne or Becker? Due to the increasing concerns regarding the COVID-19 virus for people with Duchenne [...]

COVID-19 for people affected by Duchenne or Becker #2
By Marie
In News
Posted 28 March 2020

COVID-19 for people affected by Duchenne or Becker #2

What we know about COVID-19 part 2 What do we know about COVID-19 for people affected by Duchenne or Becker? Due to the increasing concerns regarding the COVID-19 virus for people with Duchenne [...]

Edasalonexent and COVID-19
By Marie
In News, Research
Posted 27 March 2020

Edasalonexent and COVID-19

La Force is happy to share the latest edition of the Catabasis Connection newsletter. As we are all faced with an unimaginable situation, Catabasis wanted to reach out and share information in [...]

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Articles récents

  • The global day of giving
  • EMBARK, gene therapy for the treatment of DMD
  • Part B of MOMENTUM study of SRP-5051 in patients with DMD
  • World Duchenne Awareness Day 2021
  • ENDEAVOR, gene therapy for DMD

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