Giving Tuesday is your opportunity to give back… This is a day dedicated to generosity just as Black Friday and Cyber Monday are dedicated to shopping. Contributing to our cause will help [...]
2017, November 17th On a regular basis, team La Force will relay breaking news to the DMD community in News! our latest blog. We provide news highlights to give you quick-and-easy access to the [...]
The FDA has opted not to approve a treatment for DMD, ataluren from PTC Therapeutics. The FDA requires the PTC company to conduct yet another clinical trial in order to consider approval of the [...]
On September 28, 2017, the U.S. Food and Drug Administration (FDA) held an Advisory Committee (AdCom) meeting to discuss the new drug application for ataluren for oral suspension (PTC [...]
Advisory Committee (AdCom) for Translarna (ataluren) by the FDA On September 28, the US Food and Drug Administration (FDA) will hold an AdCom meeting for PTC Therapeutics Translarna (ataluren). [...]
Today, September 7th is International “Duchenne Awareness Day.” We took this opportunity to launch our video. Its aim is simply to raise awareness about Duchenne muscular dystrophy. The seventh [...]
Did you know that February is Rare Disease Month? February is Rare Disease Month DMD is also a Zebra Because it manifests itself only rarely, Duchenne muscular dystrophy (DMD) falls within the [...]
Utrophin could potentially replace dystrophin. In people with Duchenne muscular dystrophy (DMD), dystrophin does not function properly. Numerous media outlets have recently reported many exciting [...]
You CAN drive with Duchenne Muscular Dystrophy (DMD)! Being able to drive is a dream that means a lot to any teenager. Shaan Lail is living that dream. Even though he has Duchenne Muscular [...]
The FDA has just announced an unprecedented decision… The children with Duchenne muscular dystrophy were heard because it’s “yes” to Eteplirsen! Eteplirsen was approved! This is absolutely [...]