New DMD exon-skipping therapy on the way
Following positive results obtained in Phase I/II trial of SRP-4053 (Golodirsen), Sarepta Therapeutics has announced a plan to submit a new drug application (NDA) for accelerated approval of [...]
Microdystrophin gene transfer trial on Hold
Solid Biosciences announces a clinical hold on SGT-001 microdystrophin gene transfer the clinical Phase I/II clinical trial for Duchenne muscular dystrophy. Solid Biosciences Inc. announced it [...]
Canadian Research osteoprotegerin (OPG)
Meeting with professor Jérôme Frenette about osteoprotegerin (OPG). We are producing a video series of interviews with Canadian researchers working on DMD. We have met many professors, and our [...]
