Correcting nonsense mutations with CRISPR/cas9?
Correcting nonsense mutations with CRISPR / Cas9? Would it be possible to correct nonsense mutations with CRISPR/Cas9? Some patients with DMD have a point mutation (nonsense) that leads either to [...]
DAKOTA’S BIG SMILE
Notes from the “Living with DMD” web-doc Tecima Productions team. Our small production team travelled across Canada, meeting with families whose children have Duchenne muscular [...]
Positive data with vamorolone in DMD
Santhera Announces Presentation by ReveraGen of Positive 18-Month Data with Vamorolone in Duchenne Muscular Dystrophy La Force is happy to share this press release provided by Santhera [...]
Translarna™ (ataluren) Slows Disease Progression in Patients with DMD
PTC Therapeutics announces new real-world analysis demonstrating Translarna™ (ataluren) slows disease progression in patients with Duchenne muscular dystrophy La Force is happy to share [...]
PolarisDMD Trial in DMD has exceeded target enrollment
Phase 3, PolarisDMD trial of edasalonexent in DMD has exceeded target enrollment La Force is happy to share the latest edition of the Catabasis Connection newsletter Catabasis [...]
