“Chimeric cells” for DMD?
Cells Restoring dystrophin in DMD We’ve set a goal for ourselves of informing you about new treatments for Duchenne muscular dystrophy (DMD). Here are some very promising results: new research [...]
Jérôme Frenette: OPG for DMD
Jérôme Frenette: OPG for DMD Professor Jérôme Frenette, himself lost two of his children due to a genetic disease. It’s, therefore, a decision from the heart that leads him to conduct today his [...]
Understanding CRISPR/Cas9 with Jacques P. Tremblay
Canadian Research series This video series of interviews features Canadian scientists who work on solutions for Duchenne muscular dystrophy (DMD). We wish to connect you – the DMD community – [...]
Solid Biosciences announces new preclinical data about gene transfer
One of the objectives of our team is to inform you about new treatments. Here’s the latest news from a recent Solid Bioscience press release about SGT-001, the Company’s lead [...]
STAT3 a new research to treat DMD
Canadian Research series This video series of interviews features Canadian scientists who work on solutions for Duchenne muscular dystrophy (DMD). We wish to connect you – the DMD community – [...]
Capricor initiates HOPE-2 clinical trial
One of the objectives of our team is to inform you about new treatments. Here’s the latest news from a recent press released by Capricor which announces the clinical trial HOPE-2. Enjoy [...]
Edasalonexent: Positive results and no side effects
One of the objectives of our team is to inform you about new treatments. Here’s the latest news from a recent Catabasis press release about edasalonexent. Enjoy reading and thank you for [...]
A clinical trial on utrophin modulation is completed
One of the objectives of our team is to inform you about new treatments. You can catch up on the last news in the latest press release by Summit Therapeutics company about ezutromid, a utrophin [...]
Portrait of Duchenne – Every action counts!
A chance encounter launched groundbreaking DMD research When Max Sedmihradsky was two-years-old, he received the DMD diagnosis. The news was devastating beyond words for his parents Kerry and [...]
New DMD exon-skipping therapy on the way
Following positive results obtained in Phase I/II trial of SRP-4053 (Golodirsen), Sarepta Therapeutics has announced a plan to submit a new drug application (NDA) for accelerated approval of [...]
