Sarepta announces top-line results for its investigational gene therapy
Sarepta Therapeutics announces top-line results for part 1 of study 102 evaluating SRP-9001, its investigational gene therapy for the treatment of Duchenne muscular dystrophy (DMD) Jan. 7, 2021, >Original […]
Pfizer doses the first participant with Its gene therapy
Pfizer doses the first participant in phase 3 study for Duchenne muscular dystrophy (DMD) investigational gene therapy. January 07, 2021, > Original press release < Pfizer Inc. announced that the […]
Positive clinical results from MOMENTUM
Sarepta Therapeutics announces positive clinical results from MOMENTUM, a phase 2 clinical trial of SRP-5051 in patients with Duchenne muscular dystrophy amenable to skipping exon 51. Original press release > […]
The power of giving back
Giving Tuesday – the global day of giving Join us for the 8th annual Giving Tuesday on December 1rst, 2020! GivingTuesday is a global day of giving that happens each […]
The development of edasalonexent will be stopped
Catabasis Pharmaceuticals announces top-line results for the phase 3 PolarisDMD trial of edasalonexent in Duchenne muscular dystrophy. PolarisDMD Trial Did Not Achieve Primary or Secondary Endpoints – The development […]
Santhera to discontinue Phase 3 SIDEROS study
Santhera to discontinue Phase 3 SIDEROS study and development of Puldysa® in Duchenne Muscular Dystrophy (DMD) and focus on vamorolone. Original Press Release > Pratteln, Switzerland, October 6, 2020 Santhera […]
